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Mashup Score: 1
– ADPKD is the most common inherited kidney disease, with no treatments currently available that address the underlying cause of disease – – Vertex to initiate a Phase 1 clinical trial in healthy volunteers this month – – ADPKD is Vertex’s 10th disease area in the clinic, further expanding the…
Source: news.vrtx.comCategories: General Medicine News, Hem/OncsTweet
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Mashup Score: 3
– Over 8,000 patients 12 years of age and older with severe sickle cell disease or transfusion-dependent beta thalassemia may be eligible for treatment – LONDON –(BUSINESS WIRE)–Feb. 13, 2024– Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) announced today that the European Commission has…
Source: news.vrtx.comCategories: General Medicine News, CardiologistsTweet
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Mashup Score: 3
– Over 8,000 patients 12 years of age and older with severe sickle cell disease or transfusion-dependent beta thalassemia may be eligible for treatment – LONDON –(BUSINESS WIRE)–Feb. 13, 2024– Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) announced today that the European Commission has…
Source: news.vrtx.comCategories: General Medicine News, CardiologistsTweet
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Mashup Score: 3
– Over 8,000 patients 12 years of age and older with severe sickle cell disease or transfusion-dependent beta thalassemia may be eligible for treatment – LONDON –(BUSINESS WIRE)–Feb. 13, 2024– Vertex Pharmaceuticals Incorporated (Nasdaq: VRTX) announced today that the European Commission has…
Source: news.vrtx.comCategories: General Medicine News, CardiologistsTweet
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Mashup Score: 7
– Data from 75 patients with transfusion-dependent beta thalassemia or severe sickle cell disease with follow-up of up to 37.2 months continue to demonstrate that exa-cel has the potential to be a one-time functional cure – – Safety profile generally consistent with myeloablative conditioning and autologous stem cell transplant – BOSTON & ZUG,…
Source: news.vrtx.comCategories: Cardiologists, Latest HeadlinesTweet
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