Gene Therapy Trials Show Positive Results in Sickle Cell Disease and Thalassemia
Results from two early-phase trials suggest that CRISPR-Cas12a gene editing has the potential to cure sickle cell disease and transfusion-dependent beta-thalassemia.
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Animal Behavior and Cognition | bioRxiv
bioRxiv – the preprint server for biology, operated by Cold Spring Harbor Laboratory, a research and educational institution
Genetics | bioRxiv
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