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Mashup Score: 0The Sensations - Let Me In - 2 hour(s) ago
The Sensations – Let Me In, an upbeat number from the swingin early 60’s oldies post- doo wop era. Please enjoy more of the best oldies here: https://www.you…
Source: www.youtube.comCategories: General Medicine News, Rare DiseaseTweet
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Mashup Score: 1
Objective: Amyotrophic lateral sclerosis (ALS) is an incurable, progressive neurodegenerative disease with a significant health burden and poorly understood etiology. This analysis assessed the nar…
Source: www.tandfonline.comCategories: General Medicine News, Rare DiseaseTweet
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Mashup Score: 2Caring for young caregivers, a hidden population - 3 hour(s) ago
Tending to the well-being of loved ones who might fill caregiving roles, especially at vulnerable young ages, is an investment in the well-being of society at large.
Source: www.statnews.comCategories: General Medicine News, Rare DiseaseTweet
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Mashup Score: 0
Approximately 31,000 people are living with amyotrophic lateral sclerosis (ALS) in the United States, with an average of 5,000 new cases every year, according to the Centers for Disease Control and Prevention.
Source: medicalxpress.comCategories: General Medicine News, Rare DiseaseTweet
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Mashup Score: 0
Researchers successfully used a brain-computer interface to synthesize speech directly from brain activity in an ALS patient, achieving 80% word recognition accuracy by listeners, showcasing the interface’s potential for aiding communication in severe speech impairments.
Source: www.news-medical.netCategories: General Medicine News, Rare DiseaseTweet
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Mashup Score: 1Accelerated Approval: Withdrawing Gene Therapies Could Be Easier Than Small Molecules - 4 hour(s) ago
The FDA would only withdraw a rare disease gene therapy for “pretty clear” reasons, such as when there is minimal benefit with extensive side effects. The one-and-done nature of administration also makes withdrawal easier, CBER Director Peter Marks says.
Source: pink.citeline.comCategories: General Medicine News, Rare DiseaseTweet
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Mashup Score: 1For every million-dollar gene therapy, Peter Marks gets an email from FDA chief Robert Califf - 18 hour(s) ago
After Orchard Therapeutics’ gene therapy for a rare genetic disease was approved in March, Peter Marks, M.D., Ph.D., received a simple email from Commissioner Robert Califf, M.D. | After Orchard Therapeutics’ gene therapy for a rare genetic disease was approved in March, Peter Marks, M.D., Ph.D., received a simple email from Commissioner Robert Califf, M.D.
Source: www.fiercepharma.comCategories: General Medicine News, Rare DiseaseTweet
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Mashup Score: 6Working to End ALS: The State of Research and Care in the U.S. - 19 hour(s) ago
Please join Rep. Quigley and the ALS Caucus Co-Chairs, Reps. Calvert, Crow, Fitzpatrick, and Sewell, for an event highlighting research and care for ALS. ALS…
Source: www.youtube.comCategories: General Medicine News, Rare DiseaseTweet
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Mashup Score: 0
The writers who craft ad copy have learned well from poets. But the words they wield have a different intent and power.
Source: magazine.nd.eduCategories: General Medicine News, Rare DiseaseTweet
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Mashup Score: 1
Madras motor neuron disease (MMND) is a rare childhood or juvenile motor neuron disease. Herein, we present a unique case of MMND in an 18-year-old patient, which challenges the conventional und…
Source: www.cureus.comCategories: General Medicine News, Rare DiseaseTweet
For ALS scientific meetings that don't embrace interested people with ALS or caregivers -- https://t.co/I6YW9zRGv4 Please listen. cc: @TargetALS_fdn