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Mashup Score: 0Biogen Receives European Commission Approval for QALSODY® (tofersen), the First Therapy to Treat a Rare, Genetic Form of ALS | Biogen - 2 day(s) ago
The Investor Relations website contains information about Biogen’s business for stockholders, potential investors, and financial analysts.
Source: investors.biogen.comCategories: General Medicine News, Rare DiseaseTweet
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Mashup Score: 2Abstract Submission - NORD Rare Summit - 3 day(s) ago
Submission deadline – June 12, 2024 NORD notifies authors of acceptance – July 23,
Source: nordsummit.orgCategories: General Medicine News, Rare DiseaseTweet
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Mashup Score: 3
In 2015, after spending nearly four decades grinding his way up the ladder at one of the world’s most prolific construction equipment companies, Ed Rapp was nearing its apex. | Government agencies, nonprofits and dozens of biotechs have signed on to a $60 million, five-year partnership that will establish a central repository for data on ALS patients.
Source: www.fiercebiotech.comCategories: General Medicine News, Rare DiseaseTweet
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Mashup Score: 3Evidence doesn't support FDA's use of surrogate markers for accelerated approvals: report - 4 day(s) ago
In the FDA’s push to grant accelerated approvals to treat | A recent report from the Yale School of Medicine and Emory University shows that there is little evidence backing the FDA’s use of surrogate markers to determine if a medicine is fit for an accelerated approval.
Source: www.fiercepharma.comCategories: General Medicine News, Rare DiseaseTweet
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Mashup Score: 3
The US Food and Drug Administration (FDA) has published a much-awaited draft guidance detailing how it plans to implement its new platform technology designation program. Drug sponsors can use platform technologies to manufacture more than one drug or biological product through a standardized production or manufacturing process, and the program is intended to provide predictability on how they are reviewed.
Source: www.raps.orgCategories: General Medicine News, Rare DiseaseTweet
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Mashup Score: 2We’re Looking to Hire a Research Coordinator - Adult Polyglucosan Body Disease Research Foundation (APBDRF) - 4 day(s) ago
We’re looking to hire a passionate and experienced Communications and Development Manager to join our small team during this crucial period of growth in our community.
Source: www.apbdrf.orgCategories: General Medicine News, Rare DiseaseTweet
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Mashup Score: 6Rare Impact Awards - NORD's Rare Impact Awards - 4 day(s) ago
This very special event will celebrate NORD’s legacy and achievements, and honor those individuals and organizations doing remarkable work on behalf of the rare disease community.
Source: rareimpact.orgCategories: General Medicine News, Rare DiseaseTweet
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Mashup Score: 3The MED13L Foundation - 4 day(s) ago
We strive to spread awareness, provide family support, and advance medical research in search of a cure for MED13L syndrome.
Source: med13l.orgCategories: General Medicine News, Rare DiseaseTweet-
We're excited to welcome new NORD Member Organization, @Med13L_Fdn, who increase awareness of #MED13L syndrome through educational materials, awareness campaigns and advocacy. They also support patients who have a diagnosis. Learn more on their website: https://t.co/iNr6PFWvw4 https://t.co/5IZrNacQo2
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Mashup Score: 4LifeArc and ALS TDI announce partnership to develop new clinical tools for ALS and MND - PharmaTimes - 4 day(s) ago
The project will validate two minimally invasive biomarkers for ALS: MMP-9 and TIMP-1
Source: pharmatimes.comCategories: General Medicine News, Rare DiseaseTweet
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Mashup Score: 1Kurdish ALS patient kept behind bars despite severe health decline, deemed 'dangerous to society' - Stockholm Center for Freedom - 4 day(s) ago
Abdulkadir Kuday, a Kurdish inmate with amyotrophic lateral sclerosis (ALS) whose health has been deteriorating, remains imprisoned despite a Council of Forensic Medicine (ATK) report confirming he needs medical care, the Artı Gerçek news website reported. Salih Kuday, Abdulkadir’s brother, has been vocal about his brother’s dire condition, stating that he now depends on medical […]
Source: stockholmcf.orgCategories: General Medicine News, Rare DiseaseTweet
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