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Mashup Score: 0Fabry Disease and Pain - 11 month(s) ago
Jack Johnson, of the Fabry Support and Information Group (FSIG) talks about the different types of pain often associated with Fabry disease.
Source: CheckRareCategories: Hem/Onc News and Journals, Latest HeadlinesTweet
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Mashup Score: 0Fabry Disease in Females - 11 month(s) ago
Looking for information on Fabry disease? Learn about this rare X-linked lysosomal storage disorder that can affect both male and female patients. Discover characteristic symptoms, potential complications, and the latest research findings regarding female patients with Fabry disease. Find out why diagnosis can be challenging and what more research is needed to fully understand this complex…
Source: CheckRareCategories: Hem/Onc News and Journals, Latest HeadlinesTweet
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Mashup Score: 0Gene Therapy Platform Designed to Target the Heart in Fabry Disease - 11 month(s) ago
Dr. Raphael Schiffmann, of 4D Molecular Therapeutics, discusses the mechanism of action of 4D-310, a gene therapy in development to treat Cardiac symptoms in Fabry disease.
Source: CheckRareCategories: Hem/Onc News and Journals, Latest HeadlinesTweet
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Mashup Score: 0Gene Therapy For Fabry Disease Targets The Heart - 11 month(s) ago
Dr. Raphael Schiffmann, of 4D Molecular Therapeutics, discusses the cardiac effects of 4D-310, a targeted gene therapy for adults with Fabry disease.
Source: CheckRareCategories: Latest Headlines, Rare DiseaseTweet
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Mashup Score: 0New Treatments in Development for Fabry Disease - CheckRare - 11 month(s) ago
Jack Johnson, Executive Director of the Fabry Support and Information Group (FSIG) discusses the many research advances being made in Fabry disease.
Categories: Hem/Onc News and Journals, Latest HeadlinesTweet
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Mashup Score: 0Fabry Disease and Pain - 11 month(s) ago
Jack Johnson, of the Fabry Support and Information Group (FSIG) talks about the different types of pain often associated with Fabry disease.
Source: CheckRareCategories: Hem/Onc News and Journals, Latest HeadlinesTweet
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Mashup Score: 0Fabry Disease Treatment and Research Landscape - 11 month(s) ago
Dr. Ankit Mehta, from Baylor University Medical Center, discusses the treatment and research landscape for Fabry disease
Source: CheckRareCategories: Hem/Onc News and Journals, Latest HeadlinesTweet
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Mashup Score: 0Gene Therapy Platform Designed to Target the Heart in Fabry Disease - 12 month(s) ago
Dr. Raphael Schiffmann, of 4D Molecular Therapeutics, discusses the mechanism of action of 4D-310, a gene therapy in development to treat Cardiac symptoms in Fabry disease.
Source: CheckRareCategories: Hem/Onc News and Journals, Latest HeadlinesTweet
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Mashup Score: 0Fabry Disease in Females - 12 month(s) ago
Looking for information on Fabry disease? Learn about this rare X-linked lysosomal storage disorder that can affect both male and female patients. Discover characteristic symptoms, potential complications, and the latest research findings regarding female patients with Fabry disease. Find out why diagnosis can be challenging and what more research is needed to fully understand this complex…
Source: CheckRareCategories: Hem/Onc News and Journals, Latest HeadlinesTweet
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Mashup Score: 0FDA OKs New Drug for Fabry Disease - 12 month(s) ago
Pegunigalsidase alfa (Elfabrio) is an intravenously administered enzyme replacement therapy to treat adults with confirmed Fabry disease.
Source: MedscapeCategories: General Medicine News, Latest HeadlinesTweet
Jack Johnson of the Fabry Support and Information Group #FSIG, talks about the different types of pain often associated with Fabry disease #checkrare #rarediseases #fabrydisease @FabryNews @FabryOrg https://t.co/tE2Kf6dQzW