Vertex offers limited access to a cystic fibrosis drug in South Africa — and may undercut a court case
“This is not a solution for all South African patients” and is “likely to widen the disparity between rich and poor,” advocates complained.
“This is not a solution for all South African patients” and is “likely to widen the disparity between rich and poor,” advocates complained.
Zach Klaassen and Zach Reardon delve into the nuances of managing nonmetastatic castration-resistant prostate cancer (nmCRPC) in clinical practice. Dr. Reardon discusses the evolving landscape…
Two congenitally deaf children can hear after being treated with a gene therapy, according to new data from an ongoing clinical trial.
The FDA nod means trial sponsors can use Apple Watch’s A-fib history as a secondary endpoint in trials without having to do additional work.
As Americans strive to move beyond Covid-19, it is important to acknowledge that for their 7 million immunocompromised fellow citizens the pandemic continues to be…
Two congenitally deaf children can hear after being treated with a gene therapy, according to new data from an ongoing clinical trial.
FDA will host a listening session in June as part of broader work to optimize the use of, and processes, for advisory committees.
The FDA nod means trial sponsors can use Apple Watch’s A-fib history as a secondary endpoint in trials without having to do additional work.
The immense potential benefits of biotechnology are profoundly vulnerable to misuse. Better screening of synthetic DNA orders is a key barrier to bad actors.
A boy with Duchenne muscular dystrophy died after receiving a Pfizer experimental gene therapy. The company is pausing its trial in older boys.
A boy with Duchenne muscular dystrophy died after receiving a Pfizer experimental gene therapy. The company is pausing its trial in older boys.