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Gustavo A. Heresi, MD, MS, Director of the Pulmonary Vascular and Chronic Thromboembolic Pulmonary Hypertension Program in the Department of Pulmonary and Critical Care...

Gustavo A. Heresi, MD, MS, Director of the Pulmonary Vascular and Chronic Thromboembolic Pulmonary Hypertension Program in the Department of Pulmonary and Critical Care...

Ronald Oudiz, MD, FACP, FACC, FCCP, Professor of Medicine, Director, Pulmonary Hypertension Clinic, Chief, Division of Cardiology, Harbor-UCLA Medical Center, discusses pulmonary arterial hypertension...

Dr. Morava-Kozicz of the Mayo Clinic explain how the RDCRN Consortium,  FCDGC, has improves our understanding of congenital disorders of...

Dr. Angela Scheuerle, at the UT Southwestern Medical Center, discusses the importance of collaboration between clinicians to improve clinical...

Dr. Michael L. Wang, of MD Anderson Cancer Center, discusses results of the phase 3 SHINE study with newly diagnosed mantle cell lymphoma presented...

Dr. Burton discusses MPS II research highlights from WORLDSymposium...

Dr. Priya Kishnani discusses the transformational work that has been done at  Duke Health Rare Disease Center’s in changing the way we manage Pompe...

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Risdiplam’s Mechanism of Action - 1 week

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Dr. Dalia Moawad, of Genentech, explains the how risdiplam works by increasing the production SMN2 protein in spinal muscular...

Dr Katie Bishop of Acadia Pharmaceuticals explains the MOA of  trofinetide to treat Rett...