Improving the accessibility of gene therapy: developing in vivo techniques
In this video, Annarita Miccio, PhD, Imagine Institute of Genetic Diseases, Paris, France, discusses the future role of gene therapy for treating patients with hematological conditions, highlighting that new techniques should be developed to widen the eligible patient population and to decrease the costs of this therapeutic approach. For example, Dr Miccio mentions the work of her team and other groups, which aims to develop an in vivo gene therapy technique that will allow patients to forgo stem cell collection and toxic conditioning regimens. This interview took place at the 19th Annual Scientific Conference of the Academy for Sickle Cell and Thalassaemia (ASCAT 2024) in London, UK. These works are owned by Magdalen Medical Publishing (MMP) and are protected by copyright laws and treaties around the world. All rights are reserved.