Efficacy and Safety of Itepekimab for Moderate-to-Severe Asthma | NEJM
Visual Abstract from the New England Journal of Medicine — Efficacy and Safety of Itepekimab for Moderate-to-Severe Asthma
Visual Abstract from the New England Journal of Medicine — Efficacy and Safety of Itepekimab for Moderate-to-Severe Asthma
In this editorial, the authors describe the foundations of an N-of-1 gene-editing study to treat an infant with a urea-cycle disorder.
Base editors can correct disease-causing genetic variants. After a neonate had received a diagnosis of severe carbamoyl-phosphate synthetase 1 deficiency, a disease with an estimated…
In this editorial, the authors describe the foundations of an N-of-1 gene-editing study to treat an infant with a urea-cycle disorder.
In this editorial, the authors describe the foundations of an N-of-1 gene-editing study to treat an infant with a urea-cycle disorder.
Throughout the course of multiple sclerosis, gradually progressive neurologic impairment can occur, which has been called disability accrual. Current disease-modifying therapies for multiple sclero…
Quick Take Video Summary from The New England Journal of Medicine — Antiretroviral Therapy for Children with HIV in Africa
Base editors can correct disease-causing genetic variants. After a neonate had received a diagnosis of severe carbamoyl-phosphate synthetase 1 deficiency, a disease with an estimated…
Children living with human immunodeficiency virus (HIV) have limited options for second-line antiretroviral therapy (ART). In this open-label trial with a 2-by-4 factorial design, we…
Base editors can correct disease-causing genetic variants. After a neonate had received a diagnosis of severe carbamoyl-phosphate synthetase 1 deficiency, a disease with an estimated…
In this editorial, the authors describe the foundations of an N-of-1 gene-editing study to treat an infant with a urea-cycle disorder.