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Mashup Score: 0FDA Approves $3 Million Gene Therapy for Rare Brain Disorder (Cerebral Adrenoleukodystrophy) - 1 year(s) ago
Symptoms of CALD usually occur in early childhood and, if untreated, rapidly leads to severe loss of neurologic function and eventual death in most patients.
Source: CheckRareCategories: Hem/Onc News and Journals, Latest HeadlinesTweet
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Mashup Score: 0FDA Approves $3 Million Gene Therapy for Rare Brain Disorder (Cerebral Adrenoleukodystrophy) - 2 year(s) ago
Symptoms of CALD usually occur in early childhood and, if untreated, rapidly leads to severe loss of neurologic function and eventual death in most patients.
Source: CheckRareCategories: Hem/Onc News and Journals, Latest HeadlinesTweet
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Mashup Score: 0FDA Approves $3 Million Gene Therapy for Rare Brain Disorder (Cerebral Adrenoleukodystrophy) - 2 year(s) ago
Symptoms of CALD usually occur in early childhood and, if untreated, rapidly leads to severe loss of neurologic function and eventual death in most patients.
Source: CheckRareCategories: Latest Headlines, Rare DiseaseTweet
The U.S. Food and Drug Administration #FDA has granted accelerated approval for elivaldogene autotemcel #el-cel to treat males 4-17 years of age with early, active cerebral adrenoleukodystrophy #CALD https://t.co/pDy1fWLTpK