Hereditary Hemorrhagic Telangiectasia | NEJM
Images in Clinical Medicine from The New England Journal of Medicine — Hereditary Hemorrhagic Telangiectasia
Images in Clinical Medicine from The New England Journal of Medicine — Hereditary Hemorrhagic Telangiectasia
ANNEXA-I, the first ever randomised controlled trial of a reversal agent for direct oral anticoagulants, was published in 2024. The trial, which randomised patients with…
ANNEXA-I, the first ever randomised controlled trial of a reversal agent for direct oral anticoagulants, was published in 2024. The trial, which randomised patients with…
Sangamo Therapeutics said on Monday that partner Pfizer has terminated their hemophilia A gene therapy co-development agreement, sending its shares down nearly 64% in extended…
Research funded by the US National Institutes of Health (NIH) will have to be made publicly available without a period of delay,1 under the agency’s…
Action The U.S. Food and Drug Administration has approved Alhemo (concizumab-mtci) for routine prophylaxis to prevent or reduce the frequency of bleeding
Ruth Jessen Hickman, MD, is a freelance medical and science writer based in Bloomington, Indiana. Population: Roughly 1 in 200,000 people across ethnicities; may present…
Abstract. Adeno-associated virus (AAV)–based gene therapy is an emerging treatment for hemophilia A (HA) and hemophilia B (HB). In this systematic review a
A 50-year-old woman presented with a 5-year history of xanthogranulomas under her eyes. Laboratory studies were notable for thrombocytopenia and very high levels of low-density…
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Mr Brian O’Mahony, Chief Executive, Irish Haemophilia Society, recounts his experience of participating in a gene therapy…